More than two years after the Government committed to adding SMA to newborn testing, families are still waiting ...
"Monumental" is how Ashley E. Webb, MD Assistant Professor, Department of Pediatrics, Division of Child & Adolescent Neurology Neuromuscular Program Director, UTHealth, University of Texas Health ...
A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...
A couple whose son died from a rare genetic condition are encouraging others to take part in screening which they say could ...
Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...
The mother of a four-year-old boy with a rare muscle disease says screening newborn babies for the condition could "save ...
"Managing pain in patients with SMA begins with the recognition that there are predictable etiologies leading to pain in SMA and investigating them during each medical visit is important to implement ...
The singer shared an emotional update about her twins’ health on Sunday.
Newborn babies in Hull will be able to be screened for more than 200 rare genetic conditions as part of a national study to ...
LITTLE Mix star Jesy Nelson has revealed that her baby twins have been diagnosed with a severe form of Spinal Muscular Atrophy. In a heart-breaking Instagram post, the singer said her daughters could ...
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